Ko wayli
Ko Quiver Quantitative habrii, Tarsus Pharmaceuticals timmini soodugol Alkeus Pharmaceuticals ñalnde 4 settaambar. E nder soodugol ngol, Tarsus heɓi hakkeeji e winndere ndee fof e gildeuretinol acetate, ɗe mbi'etee kadi ALK-001, leɗɗe ɗe ƴeewtetee ngam ñaw Stargardt. Leɗɗe ɗee ko e hunuko njaratee, laawol gootol e ñalawma. Ɗe ngoni haa jooni e ƴeewndam NORTHSTAR tolnogal 3, ngal waɗetee e winndere ndee. Keɓe arane mawɗe ƴeewndam ngal ɗaminaa ko e hitaande 2029. FDA jaɓaani leɗɗe ɗee.
Ko waɗi ɗum teeŋti
E miijo amen, jeyɗo e ɗowooɗo golle ɗee waylii, ɗum kadi ina teeŋti. Kono ñawndugol waylaani haa jooni. Ñaw Stargardt ina waawi bonnude yi'ugol ko woni yeeso neɗɗo, ngol o huutortoo ngam janngude, heftinde yeeso yimɓe e waɗde oto. Habaar oo wi'i alaa haa jooni ñawndugol ngol FDA jaɓi ngam ñaw oo.
Ngam jooni, ina haani muñde, tawa sahaa keɓe ɗaminaa ina anndaa. Tarsus jeyi golle ɗee jooni, kono soodugol ngol timmi ɗum firtaani leɗɗe ɗe ƴeewtetee ngartii ñawndugol ngol yimɓe mbaawi heɓde. Yimɓe rewɓe kabaaruuji cellal gite ina poti seerndude ko ƴeewtagol leɗɗe holli ko addanta yaakaar e ñawndugol ngol nafoore mum tabbitinaa tee jaɓaa. Ɓe ina poti kadi haalirude naamne baɗɗe e cellal maɓɓe e ñawndoowo mo heɓi ganndal e kattanɗe ɗe potɗe.
No ɗum waawi memirde
Ko waɗata e NORTHSTAR ina ɓuri jooni memde Tarsus. Kampani oo jeyi golle ƴeewtagol leɗɗe ngam Stargardt ɗe njettii e tolnogal sakkitiingal. Ko ɗe mbaawi yottude fawii ko e no ƴeewndam ngal yahata yeeso e keɓe mum.
Ngam yimɓe wonɓe e ñaw Stargardt, ƴeewtagol leɗɗe ɗee ina jokka e ɗowgol Tarsus. Kono heɓugol leɗɗe ɗee waylataa so wonaa ƴeewndam ngal e laabi jaɓgol leɗɗe ɗee timmii e moƴƴere.
Ko waawi waɗde
Ko ɓuri yaakareede: So Tarsus jokkii e sahaa mo o habri ngam golle ɗee, ALK-001 heddoto ko leɗɗe ɗe ƴeewtetee e ɗowgol mum. NORTHSTAR jokkata ngam yottinde keɓe arane mawɗe ɗe ɗaminaa e hitaande 2029.
So golle ɗee njahii no yaakoraa: ALK-001 ina waawi ɓadaade wonde leɗɗe ɗe mbaawi suɓeede ngam ñawndugol, so NORTHSTAR hollii keɓe moƴƴe tee sarɗiiji jaɓgol ɗi ɗaɓɓaa caggal ɗum timminaa.
So golle ɗee njahaani no yaakoraa: Golle ɗee ina mbaawi waasde yahde yeeso haa leɗɗe ɗee njaɓee, so keɓe ƴeewndam ngal, ko yiytaa e no ɓandu muñirta leɗɗe ɗee walla sahaa golle ɗee ngalaa ko wallata laawol baɗangol ɗee.
Ko haani rewde yeeso
Rewee so Tarsus ina jokka wi'ude ƴeewndam NORTHSTAR ina waɗee, tee ina ɗaminaa haa jooni keɓe arane mawɗe e hitaande 2029. So keɓe ƴeewtagol leɗɗe ɗee ngasii heɓeede, rewee naatnugol ɗaɓɓitannde jaɓgol e FDA e laawol, ko FDA waɗata e ƴeewtagol ɗaɓɓitannde ndee, walla yottagol e tolno teeŋtungo e jaɓgol leɗɗe ɗee.
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